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FAST joins with University of Pennsylvania to develop investigational AAV gene therapy for Angelman syndrome - Earth News Report
The Foundation for Angelman Syndrome Therapeutics (FAST) announced today that the non-profit organization has entered into an exclusive global collaborative research and development agreement with the University of Pennsylvania to develop an investigational adeno-associated virus (AAV) gene therapy for Angelman syndrome (AS). Angelman syndrome is a nondegenerative neurogenetic disorder that is estimated to impact approximately